Gene Editing Helped One Baby—Could It Help Thousands?

基因编辑帮助了一个婴儿——它能帮助成千上万的吗?

Gloved fingers holding a small test tube and a pipette in front of many colorful bars of genetic data

Gloved fingers holding a small test tube and a pipette in front of many colorful bars of genetic data

2025-11-04  961  晦涩
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The groundbreaking clinical trial, described on 31 October in the American Journal of Human Genetics, will deploy an offshoot of the CRISPR–Cas9 gene-editing technique called base editing, which allows scientists to make precise, single-letter changes to DNA sequences. The study is expected to begin next year, after its organizers spent months negotiating with US regulators over ways to simplify the convoluted path a gene-editing therapy normally has to take before it can enter trials.

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