Megan and Ed Selser with their son, Ben, who is 2 and a half. He has Hunter syndrome, a genetic defect that eliminates an enzyme needed to break down sugar.
2026-03-05 1896词 晦涩
0:00
0:00
此音频仅限会员使用成为会员
The agency rejected the therapy last month, one in a series of denials over the last eight months that have dashed the hopes of desperate families. Though Ms. Selser’s son wasn’t a candidate for this particular gene therapy, she has been worried about other options awaiting an F.D.A. decision.
免责声明：本文来自网络公开资料，仅供学习交流，其观点和倾向不代表本站立场。